{"id":23420,"date":"2025-06-18T11:44:53","date_gmt":"2025-06-18T11:44:53","guid":{"rendered":"https:\/\/metaverseplanet.net\/blog\/?p=23420"},"modified":"2026-01-05T12:55:16","modified_gmt":"2026-01-05T12:55:16","slug":"a-world-first-a-babys-congenital-genetic-disease-treated-with-gene-editing-technology","status":"publish","type":"post","link":"https:\/\/metaverseplanet.net\/blog\/a-world-first-a-babys-congenital-genetic-disease-treated-with-gene-editing-technology\/","title":{"rendered":"A World First! A Baby&#8217;s Congenital Genetic Disease Treated with Gene-Editing Technology"},"content":{"rendered":"\n<p><strong>Doctors and scientists<\/strong> have achieved a historical first. The team successfully treated a baby&#8217;s rare disease using personalized <strong>gene-editing therapy<\/strong>.<\/p>\n\n\n\n<p><strong>Genetic diseases<\/strong> that can affect infants are among the greatest fears for parents. Now, a study conducted by a group of doctors and scientists has revealed promising results in this area. A US-based team has successfully treated a <strong>rare genetic disorder<\/strong> using a previously unheard-of method.<\/p>\n\n\n\n<p>In this study, researchers used <strong>personalized gene-editing therapy<\/strong> to treat the disease, marking a <strong>world first<\/strong>. The study findings were published in <strong>The New England Journal of Medicine<\/strong>.<\/p>\n\n\n\n<h2 class=\"wp-block-heading\"><strong>Baby Cured of High-Risk Disease Thanks to Gene-Editing Therapy<\/strong><\/h2>\n\n\n\n<figure class=\"wp-block-image size-large\"><img decoding=\"async\" width=\"1024\" height=\"576\" src=\"https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-1024x576.jpeg\" alt=\"\" class=\"wp-image-23421\" srcset=\"https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-1024x576.jpeg 1024w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-300x169.jpeg 300w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-768x432.jpeg 768w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-1536x864.jpeg 1536w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-390x220.jpeg 390w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-150x84.jpeg 150w, https:\/\/metaverseplanet.net\/blog\/wp-content\/uploads\/2025\/06\/c505dac81d57921bcce5b242673c97332289671a-scaled.jpeg 1200w\" sizes=\"(max-width: 1024px) 100vw, 1024px\" \/><\/figure>\n\n\n\n<p>The baby in this historic case, named &#8220;KJ,&#8221; had a very rare metabolic disorder called <strong>CPS 1 deficiency (carbamoyl phosphate synthetase 1 deficiency)<\/strong>. Children with this disease faced <strong>mortality rates of up to 50% in the first week<\/strong>. For those who survived, there were risks of severe brain problems, mental and developmental delays, and the need for liver transplantation.<\/p>\n\n\n\n<p>The research team developed a <strong>CRISPR-based, personalized gene-editing therapy<\/strong> specifically for this baby, a technology that directly edits human DNA. This allowed a mutation in the patient&#8217;s DNA to be corrected using <strong>CRISPR technology<\/strong>, leading to successful outcomes.<\/p>\n\n\n\n<p>This achievement has the potential to be groundbreaking as a world first. In the future, we may see more <strong>personalized gene-editing therapies<\/strong>. This technology could be used to treat many different types of diseases and save lives.<\/p>\n\n\n\n<h3 class=\"wp-block-heading\">You Might Also Like;<\/h3>\n\n\n<ul class=\"wp-block-latest-posts__list wp-block-latest-posts\"><\/ul>","protected":false},"excerpt":{"rendered":"<p>Doctors and scientists have achieved a historical first. The team successfully treated a baby&#8217;s rare disease using personalized gene-editing therapy. Genetic diseases that can affect infants are among the greatest fears for parents. Now, a study conducted by a group of doctors and scientists has revealed promising results in this area. A US-based team has &hellip;<\/p>\n","protected":false},"author":1,"featured_media":23422,"comment_status":"open","ping_status":"closed","sticky":false,"template":"","format":"standard","meta":{"googlesitekit_rrm_CAown96uCw:productID":"","footnotes":""},"categories":[336],"tags":[340],"class_list":["post-23420","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-futurescience","tag-science-news"],"amp_enabled":true,"_links":{"self":[{"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/posts\/23420","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/comments?post=23420"}],"version-history":[{"count":0,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/posts\/23420\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/media\/23422"}],"wp:attachment":[{"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/media?parent=23420"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/categories?post=23420"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/metaverseplanet.net\/blog\/wp-json\/wp\/v2\/tags?post=23420"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}